Valproic Acid in Ambulant Adults With Spinal Muscular Atrophy

PHASE2CompletedINTERVENTIONAL
Enrollment

33

Participants

Timeline

Start Date

July 31, 2007

Primary Completion Date

December 31, 2009

Study Completion Date

November 30, 2010

Conditions
Spinal Muscular Atrophy
Interventions
DRUG

Valproic Acid (VPA)

Drug: Valproic Acid and Levocarnitine; capsules

DRUG

Placebo

For six months, pts are randomized into placebo or treatment. After 6 months, all pts are on treatment

Trial Locations (1)

43210

Ohio State University Medical Center, Dept. of Neurology, Columbus

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Families of Spinal Muscular Atrophy

OTHER

collaborator

Abbott

INDUSTRY

lead

University of Utah

OTHER