Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin (AAT) Deficiency

PHASE1CompletedINTERVENTIONAL
Enrollment

9

Participants

Timeline

Start Date

February 28, 2006

Primary Completion Date

January 31, 2015

Study Completion Date

January 31, 2015

Conditions
Alpha 1-Antitrypsin Deficiency
Interventions
BIOLOGICAL

rAAV1-CB-hAAT

Trial Locations (2)

32610

University of Florida, College of Medicine, Department of Pediatrics, Gainesville

01655

University of Massachusetts School of Medicine, Worcester

Sponsors
All Listed Sponsors
collaborator

National Heart, Lung, and Blood Institute (NHLBI)

NIH

collaborator

Beacon Therapeutics

INDUSTRY

collaborator

Alpha-1 Foundation

OTHER

collaborator

University of Florida

OTHER

collaborator

National Center for Research Resources (NCRR)

NIH

lead

University of Massachusetts, Worcester

OTHER