50
Participants
Start Date
July 31, 2006
Primary Completion Date
March 31, 2007
Study Completion Date
March 31, 2007
Blood sample
New York University School of Medicine, Neurogenetics Department, New York
Children's Hospital of Philadelphia, Philadelphia
National Institute of Neurological Disorders and Stroke, NIH, Bethesda
Emory University Lysosomal Storage Disease Center, Decatur
University Research Foundation for Lysosomal Storage Diseases, Inc., Coral Springs
Lysosomal Disease Center, Cincinnati Children's Hospital, Cincinnati
University of California - San Francisco, San Francisco
Lead Sponsor
Amicus Therapeutics
INDUSTRY