19
Participants
Start Date
December 31, 2006
Primary Completion Date
July 31, 2007
Study Completion Date
July 31, 2007
PTC124
4-,4-, and 8-mg/kg PO first 14 days 10-, 10-, and 20-mg/kg TID second 14 days
Hadassah University Hospital - Mount Scopus, Jerusalem
Lead Sponsor
PTC Therapeutics
INDUSTRY