24
Participants
Start Date
September 30, 2005
Primary Completion Date
August 31, 2006
Study Completion Date
August 31, 2006
PTC124
Johns Hopkins Hospital, Baltimore
Rainbow Babies and Children's Hospital, Cleveland
The Children's Hospital, Denver
University of Alabama at Birmingham, Birmingham
Stanford University Medical Center, Palo Alto
Lead Sponsor
Cystic Fibrosis Foundation
OTHER
FDA Office of Orphan Products Development
FED
PTC Therapeutics
INDUSTRY