PTC124 for Cystic Fibrosis

PHASE2CompletedINTERVENTIONAL
Enrollment

24

Participants

Timeline

Start Date

September 30, 2005

Primary Completion Date

August 31, 2006

Study Completion Date

August 31, 2006

Conditions
Cystic Fibrosis
Interventions
DRUG

PTC124

Trial Locations (5)

21287

Johns Hopkins Hospital, Baltimore

44106

Rainbow Babies and Children's Hospital, Cleveland

80218

The Children's Hospital, Denver

35233-1711

University of Alabama at Birmingham, Birmingham

94304-5786

Stanford University Medical Center, Palo Alto

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

Cystic Fibrosis Foundation

OTHER

collaborator

FDA Office of Orphan Products Development

FED

lead

PTC Therapeutics

INDUSTRY