Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy

PHASE2CompletedINTERVENTIONAL
Enrollment

94

Participants

Timeline

Start Date

September 30, 2005

Primary Completion Date

November 30, 2007

Study Completion Date

November 30, 2007

Conditions
Spinal Muscular Atrophy
Interventions
DRUG

Valproic Acid and Levocarnitine

VPA,sprinkle cap; Levocarnitine, syrup; dosage is by weight

DRUG

Placebo

Trial Locations (6)

21287

Johns Hopkins University, Baltimore

48201

Children's Hospital of Michigan, Detroit

84132

University of Utah/Primary Children's Medical Center, Salt Lake City

43210-1228

Ohio State University, Columbus

53792-9988

University of Wisconsin Children's Hospital, Madison

H3T 1C5

Hospital Sainte-Justine, Montreal

Sponsors
All Listed Sponsors
collaborator

Families of Spinal Muscular Atrophy

OTHER

collaborator

Leadiant Biosciences, Inc.

INDUSTRY

collaborator

Abbott

INDUSTRY

lead

University of Utah

OTHER