Stem Cell Transplant w/Laronidase for Hurler

PHASE2CompletedINTERVENTIONAL
Enrollment

25

Participants

Timeline

Start Date

March 31, 2004

Primary Completion Date

November 30, 2012

Study Completion Date

November 30, 2012

Conditions
Mucopolysaccharidosis IHurler Syndrome
Interventions
PROCEDURE

Stem Cell Transplant

enzyme replacement 10-12 weeks prior to hematopoietic stem cell transplant (HSCT), and 8 weeks following

DRUG

Laronidase ERT

Laronidase ERT will be administered 10-12 weeks prior to HSCT, and 8 weeks following.

Trial Locations (1)

55455

Masonic Cancer Center, University of Minnesota, Minneapolis

All Listed Sponsors
lead

Masonic Cancer Center, University of Minnesota

OTHER

NCT00176891 - Stem Cell Transplant w/Laronidase for Hurler | Biotech Hunter | Biotech Hunter