NCT00004294View on ClinicalTrials.gov

Phase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher Disease

PHASE1CompletedINTERVENTIONAL
Enrollment

15

Participants

Timeline

Start Date

November 30, 1999

Conditions
Gaucher's Disease
Interventions
GENETIC

human glucocerebrosidase gene into autologous peripheral blood stem cells

Trial Locations (1)

15260

University of Pittsburgh, Pittsburgh

All Listed Sponsors
collaborator

National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

NIH

collaborator

University of Pittsburgh

OTHER

lead

National Center for Research Resources (NCRR)

NIH