About
Gene Therapy
Areas of Focus
Categories
Gene Therapy, RNA & Peptide TherapyBiotech
Clinical Trials (6)
View allTotal Trials
6
As Lead Sponsor
4
As Collaborator
2
Total Enrollment
130
By Phase
PHASE1/PHASE2: 3
By Status
RECRUITING: 4TERMINATED: 1UNKNOWN: 1
Clinical Trials Pipeline6 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2019
2020
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
2032
Today
Hover over trial bars to see details
Recent Trials
NCT05419492Lead Sponsor
A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome
PHASE1/PHASE2Recruiting
22 participants
Started: May 14, 2024 · Completed: Apr 30, 2031
NCT06283212Lead Sponsor
A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome
PHASE1/PHASE2Recruiting
4 participants
Started: May 9, 2024 · Completed: Sep 30, 2030
NCT06112275Lead Sponsor
A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children with SCN1A-positive Dravet Syndrome (Australia Only)
PHASE1/PHASE2Recruiting
4 participants
Started: Feb 28, 2024 · Completed: Jun 30, 2030
NCT05651204Collaborator
GABA Biomarkers in Dravet Syndrome
N/ARecruiting
36 participants
Started: Sep 8, 2022 · Completed: Sep 8, 2027
NCT04537832Lead Sponsor
Natural History Study of Infants and Children With Developmental and Epileptic Encephalopathies
N/ATerminated
58 participants
Started: Jan 18, 2021 · Completed: Mar 31, 2023
Locations (1)
Headquarters
South SF, CA, United States
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