Rare Genetic Diseases
Total Trials
8
As Lead Sponsor
As Collaborator
0
Total Enrollment
191
NCT02807961
Safety, Tolerability, Pharmacokinetics of ELX-02 in Healthy Adult Volunteers
Phase: Phase 1
Role: Lead Sponsor
Start: Jul 31, 2016
Completion: May 31, 2017
NCT03292302
Phase 1 Study of ELX-02 in Healthy Adults
Start: Sep 26, 2017
Completion: Dec 15, 2017
NCT03309605
Phase 1 Study of ELX-02 in Healthy Adult Subjects
Start: Oct 11, 2017
Completion: Jul 17, 2019
NCT03776539
A Study to Evaluate the Effects of Renal Impairment on the Pharmacokinetics of ELX-02
Start: Jan 4, 2019
Completion: Aug 7, 2019
NCT04069260
A Phase 2 Study of ELX-02 in Patients With Nephropathic Cystinosis
Phase: Phase 2
Start: Aug 2, 2019
Completion: Dec 17, 2019
NCT04126473
A Phase 2 Study to Evaluate the Safety, Tolerability, PK and PD in Cystic Fibrosis Patients With at Least 1 G542X Allele
Start: Nov 5, 2019
Completion: Apr 6, 2022
NCT04135495
A Phase 2 Study to Evaluate the Safety, Tolerability, PK and PD of ELX-02 in Cystic Fibrosis Patients With G542X Allele
Start: Nov 25, 2019
Completion: Oct 3, 2022
NCT05448755
A Study of ELX-02 in Patients With Alport Syndrome
Start: Nov 28, 2022
Completion: May 30, 2023
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